NHS to use world's most expensive drug to treat spinal muscular atrophy

NHS to use world's most expensive drug to treat spinal muscular atrophy:

Zolgensma, which costs £1.79m for one-off treatment, will be available in England this year for the first time

The world’s most expensive drug, which treats babies and young children with a rare and often fatal degenerative disorder, will be available this year for the first time on the NHS in England.

Zolgensma, which costs £1.79m per dose, halts the progression of spinal muscular atrophy (SMA), which involves loss of movement, muscle weakness and paralysis, and is the leading genetic cause of death in infants.

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